Duchenne UK’s Project HERCULES awarded prestigious rare disease award

Nov 2, 2018

Project HERCULES is a unique international multi-stakeholder collaborative project set up by Duchenne UK to develop tools and evidence to support Health Technology Assessment (HTA) and reimbursement decisions for new treatments for Duchenne Muscular Dystrophy (DMD). It brings together eight leading pharmaceutical companies, academics, patient organisations and advisers to develop and build a better evidence base for DMD to aid the pricing and reimbursement stage of drug development. Source Health Economics are developing the core economic model for this collaboration.

This collaboration was recognised by the EURORDIS Black Pearl Company Award for Patient Engagement.

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